Overcoming the blood-brain barrier: therapy delivery for Sanfilippo

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Frontiers CNS-Targeting Therapies for Lysosomal Storage Diseases

The battle of lipid-based nanocarriers against blood-brain barrier

Strategies for delivering therapeutics across the blood–brain

MPS III Sanfilippo Syndrome - Flipbook by National MPS Society

Targeting the central nervous system in lysosomal storage diseases

MPS Treatment Strategies to Cross Blood-Brain Barrier Reviewed in

Mannose 6-Phosphate Receptor–mediated Transport of Sulfamidase

Blood-Brain Barrier (BBB)-Crossing Strategies for Improved

Pharmaceutics, Free Full-Text

Frontiers Pre-clinical Mouse Models of Neurodegenerative Lysosomal Storage Diseases

Sci. Pharm., Free Full-Text

Sanfilippo Children's Foundation - Research News