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Frontiers CNS-Targeting Therapies for Lysosomal Storage Diseases
The battle of lipid-based nanocarriers against blood-brain barrier
Strategies for delivering therapeutics across the blood–brain
MPS III Sanfilippo Syndrome - Flipbook by National MPS Society
Targeting the central nervous system in lysosomal storage diseases
MPS Treatment Strategies to Cross Blood-Brain Barrier Reviewed in
Mannose 6-Phosphate Receptor–mediated Transport of Sulfamidase
Blood-Brain Barrier (BBB)-Crossing Strategies for Improved
Pharmaceutics, Free Full-Text
Frontiers Pre-clinical Mouse Models of Neurodegenerative Lysosomal Storage Diseases
Sci. Pharm., Free Full-Text
Sanfilippo Children's Foundation - Research News